Gene Therapy for Spinal Muscular Atrophy (SMA): A Review of Current Challenges and Safety Considerations for Onasemnogene Abeparvovec (Zolgensma)

Tolu Ogbonmide; Rajni Rathore; Shahid B. Rangrej; Stedrea  Hutchinson; Marcia  Lewis; Stephenie  Ojilere; Victoria  Carvalho; Irenaissia  Kelly; Tolu S. Ogbonmide; Rajni Rathore; Shahid B. Rangrej; Stedrea  Hutchinson; Marcia  Lewis; Stephenie  Ojilere; Victoria  Carvalho; Irenaissia  Kelly

doi:10.7759/cureus.36197

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